The Genes
A detailed list of US trials is directly available on the GeMCRIS web site
HealthValue

AIDS
Cystic fibrosis
Peripheral Arterial Disease
Coronary diseases
Congenital Immune

Deficiencies
Hemophilia
Fanconi's anemia
As of January 2012 more than 1100 gene therapy clinical trials have been performed worldwide.
By order of frequency these trials bear on :
Gene therapy means introducing into our cells a gene. This is done because the normal gene is absent or dysfunctional, or because we need a gene to activate a repair process (vascular diseases), or because the gene will directly or after stimulation attack a disease (cancer, Aids). Introduction of the gene into the body requires innocuous vectors : certain viruses, ou circular fragments of DNA called plasmids, like those used for manufacturing recombinant proteins
Gene
Therapy
PROTEINS